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UK Scientists Led The Trial Of AMT-130, The First Gene Therapy Tested In Humans For Huntington’s. Developed By uniQure, It Reduces Toxic Huntingtin Protein. In A 3-Year, 29-Person Study, High-Dose Patients Saw 75% Slower Progression. Results Were Measured Via Motor/Cognitive Tests And Spinal Fluid Markers. FDA Filing Is Expected Early 2026.

First promising gene therapy for incurable brain disease discovered by scientists | Fox News

https://www.foxnews.com/health/scientists-may-have-discovered-first-gene-therapy-incurable-brain-disease

Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington’s disease, with FDA approval application planned for early next year.